Study Details

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Gene Transfer Study in Patients with Late Onset Pompe Disease

This trial is recruiting
The study is currently recruiting participants.

Clinicaltrials.gov ID

The unique identification code given to each clinical study upon registration at ClinicalTrials.gov.
NCT04174105

Astellas Study ID

The unique identification code given by the study sponsor.

AT845-01

EudraCT ID

The unique identification code given to each clinical study upon registration at EudraCT (European Union Drug Regulating Authorities Clinical Trials Database).

2019-003595-38

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Condition

Pompe Disease

Phase

These clinical trials are usually the first time an experimental treatment is studied in a small group of people.

Phase 1

Age

18 Years - 80 Years

Sex

Female & Male

Product

N/A

Type

A type of clinical study in which participants are assigned to groups that receive one or more intervention/treatment (or no intervention) so that researchers can evaluate the effects of the interventions on biomedical or health-related outcomes.

Interventional

Trial Dates

Oct 2020 - May 2029

Masking

None (Open Label)

Enrollment number

12

A Phase 1/2, Open-Label, Ascending-Dose Clinical Study to Evaluate the Safety and Preliminary Efficacy of AT845, an AAV8-Delivered Gene Transfer Therapy in Patients with Late Onset Pompe Disease

Study summary

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Would you like more information about clinical trial sites that are recruiting participants for Gene Transfer Study in Patients with Late Onset Pompe Disease? Contact us by filling our your information to the right and we’ll respond to you.

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Locations

University of California Irvine, Department of Neurology

Orange, United States, 92868

Recruiting
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Stanford University

Palo Alto, United States, 94304

Recruiting
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University of Utah, Division of Medical Genetics

Salt Lake City, United States, 84108

Recruiting
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Newcastle Upon Tyne Hospitals Foundation Trust Clinical Research Facility

Newcastle upon Tyne, United Kingdom, NE1 4LP

Recruiting
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